Robert Bell’s Post

🇺🇲 Honoring the Brave: This Memorial Day, we pay tribute to the heroes who made the ultimate sacrifice to defend our freedom. Join us in remembering and honoring the courageous men and women who selflessly served our nation. #MemorialDay 📸: Memorial Day Flag Garden on the Boston Common, organized by the Massachusetts Military Heroes Fund

If you’re at #ASGCT23, don’t miss our oral presentation at 9am PT tomorrow on how we’re rewriting 𝘈𝘉𝘊𝘈4 RNA for the treatment of Stargardt disease. These data could have therapeutically meaningful implications for patients with Stargardt disease, the most common form of inherited macular degeneration, as well as other diseases that are not addressable by today’s gene therapy and gene editing technologies. More than a quarter of a century has passed since the cause of Stargardt disease was discovered, and this is the first report quantifying and confirming therapeutically relevant levels of full-length 𝘈𝘉𝘊𝘈4 protein produced after a single dose in a large animal. With durable editing now confirmed in non-human primates and replicated in human retinal explants, Ascidian is currently in IND-enabling studies advancing towards clinical development. Find our presentation details here 👇 https://bit.ly/3MBG592 #GeneTherapy #Stargardt #RewritingRNA #TeamAscidian American Society of Gene & Cell Therapy Robert Bell Romesh Subramanian

Ascidian is hiring! We are looking for a scientist to join our amazing discovery team!